Natural History, Outcome, and Treatment Efficacy in Children and Adults with Glutaryl-CoA Dehydrogenase Deficiency
- Stefan Kölker
- , Sven F Garbade
- , Cheryl R Greenberg
- , James V Leonard
- , Jean-Marie Saudubray
- , Antonia Ribes
- , H Serap Kalkanoglu
- , Allan M Lund
- , Begoña Merinero
- , Moacir Wajner
- , Mónica Troncoso
- , Monique Williams
- , John H Walter
- , Jaume Campistol
- , Milagros MartÍ-Herrero
- , Melissa Caswill
- , Alberto B Burlina
- , Florian Lagler
- , Esther M Maier
- , Bernd Schwahn
- , Aysegul Tokatli
- , Ali Dursun
- , Turgay Coskun
- , Ronald A Chalmers
- , David M Koeller
- , Johannes Zschocke
- , Ernst Christensen
- , Peter Burgard
- , Georg F Hoffmann
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